Dec 8, 2021
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Michael Yeaman, PhD, chief medical advisor to the Guthy-Jackson Charitable Fund, based in Los Angeles. Dr. Yeaman speaks about neuromyelitis optica spectrum disorder (NMOSD), a rare autoimmune disease that was once thought to be a form of...
Nov 29, 2021
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Donald S. Wood, PhD, president and CEO of the Muscular Dystrophy Association (MDA). Their conversation focuses on the latest therapies for Duchenne muscular dystrophy, Pompe disease, and spinal muscular atrophy, and on the upcoming 2022 MDA...
Nov 18, 2021
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Cori Forster, vice-president of the Cold Agglutinin Disease Foundation (CADF) — a nonprofit organization formed to advocate for patients and families affected by CAD. We also talk about research on new therapies for this extremely rare...
Nov 9, 2021
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Amir London, CEO of Israel's Kamada — a major biopharmaceutical company that already has an FDA-approved therapy for alpha-1 antitrypsin deficiency, and is now pursuing an inhaled AAT drug for the same...
Nov 3, 2021
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Dr. Haggi Mazeh, an endocrine surgeon at Hebrew University's Hadassah Medical Center in Jerusalem. Dr. Mazeh, one of Israel's top experts on thyroid cancer, talks extensively about the challenges of treating medullary thyroid...