Sep 24, 2021
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Doug Kerr, MD, PhD, chief medical officer at Generation Bio in Cambridge, Massachusetts. The company is aggressively pursuing redosable gene therapies for hemophilia and other...
Sep 23, 2021
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Jerry Vockley, MD, PhD, chief of medical genetics at Pennsylvania's UPMC Children's Hospital of Pittsburgh. Dr. Vockley is also the founder of INFORM, the International Network for Fatty Acid Oxidation Research and Management, which will hold its...
Sep 22, 2021
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Hagit Baris-Feldman, MD, director of the Genetics Institute at Israel's Tel Aviv Sourasky Medical Center. Dr. Baris-Feldman, who also chairs the Israel Medical Genetics Association and is an associate professor at Tel Aviv University's Sackler...
Sep 17, 2021
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Noah Greenspan, DPT, founder of New York City's Pulmonary Wellness & Rehabilitation Center. Dr. Greenspan, who also runs the nonprofit Pulmonary Wellness Foundation, talks about diagnosing and treating pulmonary arterial...
Sep 13, 2021
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Barry Byrne, MD, director of the University of Florida's Powell Gene Therapy Center in Gainesville. Dr. Byrne has spent years researching potential gene therapies for Pompe disease, comments on the FDA's recent approval of avalglucosidase...